Pfizer’s perseverance towards rare disease treatments

What is people’s recognition about ‘rare disease’? Normally, they think it is a disease that is uncommon, hard to be cured and have a high mortality rate.

They are not totally wrong. A rare disease appears when they are an infant or children on a half of rare disease/disorder patients, and 30% of them die before the age of 5, which causes population-social losses. In particular, there are abou...